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Duchenne muscular dystrophy

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Search Period All yearsLast 12 monthsLast 5 years Topic All topicsGeneralNutrition and dietAlternative treatment methods Type of research Any type of researchHighest level of evidence only (36)Meta-analysis (9)Randomized trial (11)Systematic review (9)Phase 3 study (7)Clinical examination (506)Review article (205)Early study (phase 1 or 2) (27)Case report (101)Laboratory or animal study (64)Commentary or editorial (52)Retracted Publication (4) Studies Currently Seeking Participants Only (38)

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Publications and studies (1744)

• Clinical trialiResearch in patients, without randomization between groups. Useful, but less certain than a randomized trial. Study of Eteplirsen in DMD Patients (2021-01-25) ♡
• Clinical trialiResearch in patients, without randomization between groups. Useful, but less certain than a randomized trial. Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy (2021-01-25) ♡
• Clinical trialiResearch in patients, without randomization between groups. Useful, but less certain than a randomized trial. Safety and Efficacy Study of IGF-1 in Duchenne Muscular Dystrophy (2021-01-20) ♡
• Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Transaminitis in a Three-year-old Boy with Duchenne Muscular Dystrophy. (2020/12/28) ♡
• Aberrant RhoA activation in macrophages increases senescence-associated secretory phenotypes and ectopic calcification in muscular dystrophic mice. (2020/12/23) ♡
• Laboratory or animal researchiNo research in humans yet. Promising in a test tube or in mice unfortunately means nothing for patients. Detailed genetic and functional analysis of the hDMDdel52/mdx mouse model. (2020/12/23) ♡
• Commentary or editorialiAn expert's opinion or commentary, not new research. Decoding DMD transcriptional networks using single-nucleus RNA sequencing. (2020/12/22) ♡
• Confined placental mosaicism of Duchenne muscular dystrophy: a case report. (2020/12/17) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Current Genetic Survey and Potential Gene-Targeting Therapeutics for Neuromuscular Diseases. (2020/12/16) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Combined Cell Therapy in the Treatment of Neurological Disorders. (2020/12/15) ♡
• Nitric Oxide (NO) and Duchenne Muscular Dystrophy: NO Way to Go? (2020/12/13) ♡
• Clinical trialiResearch in patients, without randomization between groups. Useful, but less certain than a randomized trial. T(1)-Mapping and extracellular volume estimates in pediatric subjects with Duchenne muscular dystrophy and healthy controls at 3T. (2020/12/10) ♡
• The Failed Clinical Story of Myostatin Inhibitors against Duchenne Muscular Dystrophy: Exploring the Biology behind the Battle. (2020/12/10) ♡
• Gene modification strategies using AO-mediated exon skipping and CRISPR/Cas9 as potential therapies for Duchenne muscular dystrophy patients. (2020/12/09) ♡
• PMO-based let-7c site blocking oligonucleotide (SBO) mediated utrophin upregulation in mdx mice, a therapeutic approach for Duchenne muscular dystrophy (DMD). (2020/12/09) ♡
• The role of Nrf2 in acute and chronic muscle injury. (2020/12/08) ♡
• Systematic reviewiAll research on one question is searched according to fixed rules and compared side by side, so that no studies with poor outcomes are missed. The Use of Virtual Reality Technologies in the Treatment of Duchenne Muscular Dystrophy: Systematic Review. (2020/12/08) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Cellular dynamics of myogenic cell migration: molecular mechanisms and implications for skeletal muscle cell therapies. (2020/12/07) ♡
• Effects of Bisphosphonate Therapy on Bone Mineral Density in Boys with Duchenne Muscular Dystrophy. (2020/12/06) ♡
• Commentary or editorialiAn expert's opinion or commentary, not new research. Treatment with Ataluren for Duchenne Muscular Dystrophy. (2020/12/04) ♡
• Description of a Novel Mechanism Possibly Explaining the Antiproliferative Properties of Glucocorticoids in Duchenne Muscular Dystrophy Fibroblasts Based on Glucocorticoid Receptor GR and NFAT5. (2020/12/03) ♡
• Propelling Healthcare with Advanced Therapy Medicinal Products: A Policy Discussion. (2020/12/03) ♡
• Tasks and interfaces in primary and specialized palliative care for Duchenne muscular dystrophy - A patients' perspective. (2020/12/01) ♡
• Laboratory or animal researchiNo research in humans yet. Promising in a test tube or in mice unfortunately means nothing for patients. Generation of three Duchenne Muscular Dystrophy patient-specific induced pluripotent stem cell lines DMD_YoTaz_PhyMedEXp, DMD_RaPer_PhyMedEXp, DMD_OuMen_PhyMedEXp (INSRMi008-A, INSRMi009-A and INSRMi010-A). (2020/12/01) ♡
• Nature and Predictors of Response Changes in Modified-Delphi Panels. (2020/12/01) ♡
• Early-stage study (phase 1 or 2)iEarly research in a small group, primarily aimed at safety and dosage. Whether it actually works still needs to be determined afterward. Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study. (2020/12/01) ♡
• Commentary or editorialiAn expert's opinion or commentary, not new research. [Pluripotent stem cells lacking dystrophin transformed into cardiomyocytes]. (2020/12/01) ♡
• Causes of clinical variability in Duchenne and Becker muscular dystrophies and implications for exon skipping therapies. (2020/12/01) ♡
• Giovanni Nigro and the Naples's school: historical contribution to the knowledge of heart involvement in Duchenne/Becker muscular dystrophies. (2020/12/01) ♡
• Impaired myocardial strain in early stage of Duchenne muscular dystrophy: its relation with age and motor performance. (2020/12/01) ♡
• Quadriceps muscle strength in Duchenne muscular dystrophy and effect of corticosteroid treatment. (2020/12/01) ♡
• Effects of Bisphosphonates on Osteoporosis Induced by Duchenne Muscular Dystrophy: A Prospective Study. (2020/12/01) ♡
• RENAL, HEPATIC AND IMMUNE FUNCTION INDICES IN PATIENTS WITH DUCHENNE MUSCULAR DYSTROPHY. (2020/12/01) ♡
• BETs inhibition attenuates oxidative stress and preserves muscle integrity in Duchenne muscular dystrophy. (2020/11/30) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Of rAAV and Men: From Genetic Neuromuscular Disorder Efficacy and Toxicity Preclinical Studies to Clinical Trials and Back. (2020/11/28) ♡
• Tetraspanin CD82 is necessary for muscle stem cell activation and supports dystrophic muscle function. (2020/11/27) ♡
• Echocardiographic signs of subclinical cardiac function impairment in Duchenne dystrophy gene carriers. (2020/11/27) ♡
• Genotype-Phenotype Correlations in Duchenne and Becker Muscular Dystrophy Patients from the Canadian Neuromuscular Disease Registry. (2020/11/23) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Tiny Regulators of Massive Tissue: MicroRNAs in Skeletal Muscle Development, Myopathies, and Cancer Cachexia. (2020/11/23) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. New Therapeutics Options for Pediatric Neuromuscular Disorders. (2020/11/23) ♡
• Is It Possible for Children in Duchenne Muscular Dystrophy to Preserve Cardiac Function with Medical Assistance? (2020/11/22) ♡
• Validity of bioelectrical impedance to estimate fat-free mass in boys with Duchenne muscular dystrophy. (2020/11/20) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. A Role for Caveolin-3 in the Pathogenesis of Muscular Dystrophies. (2020/11/19) ♡
• The Effect of Deflazacort Treatment on the Functioning of Skeletal Muscle Mitochondria in Duchenne Muscular Dystrophy. (2020/11/19) ♡
• Improved transduction of canine X-linked muscular dystrophy with rAAV9-microdystrophin via multipotent MSC pretreatment. (2020/11/17) ♡
• Corrigendum: Serum MyomiRs as Biomarkers for Female Carriers of Duchenne/Becker Muscular Dystrophy. (2020/11/12) ♡
• Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Recurrent Exercise-Induced Rhabdomyolysis in a Healthy Adolescent Girl. (2020/11/12) ♡
• Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. SG1002 and Catenated Divalent Organic Sulfur Compounds as Promising Hydrogen Sulfide Prodrugs. (2020/11/10) ♡
• Laboratory or animal researchiNo research in humans yet. Promising in a test tube or in mice unfortunately means nothing for patients. Investigation of the effect of taurine supplementation on muscle taurine content in the mdx mouse model of Duchenne muscular dystrophy using chemically specific synchrotron imaging. (2020/11/09) ♡
• Decreasing HepG2 Cytotoxicity by Lowering the Lipophilicity of Benzo[d]oxazolephosphinate Ester Utrophin Modulators. (2020/11/04) ♡

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