Duchenne muscular dystrophy
Would you like to receive a message when there is new research on Duchenne muscular dystrophy? This is possible with an account. Create a free account or log in.
Automatically tracked from PubMed and ClinicalTrials.gov, newest on top. Nothing ever disappears here: what you keep in your favorites remains findable. · RSS feed of this disease · only the strongest evidence
Read in plain language what each study is about? With Premium, above every publication you'll see one sentence explaining what was studied — and you'll get notified as soon as there's new research on Duchenne muscular dystrophy. View what Premium costs.
Publications and studies (1744)
- Evaluation of a serum protein signature as monitoring biomarker for Duchenne muscular dystrophy in a long-term clinical trial with corticosteroids. (2026/07/13) ♡
- Clinical, pathological, and genetic characteristics of 23 DMD patients in northern China. (2026/07/13) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Navigating sexual health, fertility, and adult wellness in individuals with Duchenne muscular dystrophy: Current standards of care and future directions. (2026/07/13) ♡
- Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Fat Embolism Syndrome Following Elective Orthopedic Surgery in a Patient With Duchenne Muscular Dystrophy. (2026/07/10) ♡
- Commentary or editorialiAn expert's opinion or commentary, not new research. Rewriting Duchenne muscular dystrophy therapy. (2026/07/09) ♡
- Real-world safety profile of givinostat: an early post-marketing pharmacovigilance study based on the FAERS database. (2026/07/09) ♡
- Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Case Report: The effect of early initiation of eteplirsen treatment on the cardiac and motor disease course in an individual with Duchenne muscular dystrophy. (2026/07/09) ♡
- Development and Validation of a Novel, Disease-Specific, Caregiver-Reported Outcome Measure: The Duchenne Muscular Dystrophy Caregiver Reported-Health Index (DMDCR-HI). (2026/07/08) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Convergent innate immune and regulated cell-death pathways in selected myopathies. (2026/07/08) ♡
- GDF5 modulation of MuSC pool as a potential therapeutic benefit for DMD. (2026/07/07) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Systemic regeneration medicines for muscular dystrophy: progress and challenges in pro-regenerative drug development. (2026/07/06) ♡
- IMU-based workspace area as a promising complementary tool to assess upper limb function in Neuromuscular diseases: A one-year follow-up. (2026/07/06) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. The role of Piezo1 in skeletal muscle physiology and pathology: from mechanosensing to precision therapy. (2026/07/05) ♡
- Disease progression and economic burden of duchenne muscular dystrophy: A retrospective study using Swedish register data. (2026/07/04) ♡
- Fat-Fraction Quantification Using Three-Point Dixon Technique in Duchenne Muscular Dystrophy and Its Correlation With Clinical Progression and Genotypic Characteristics: A Single Centre One-Year Prospective Study. (2026/07/03) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Virtual Reality-Based Rehabilitation in Children and Adolescents with Muscular Dystrophy: A Systematic Review of Feasibility, Engagement, and Clinical Outcomes. (2026/07/03) ♡
- Microdystrophins partially rescue deficits of duchenne muscular dystrophy iPSC-cardiomyocytes. (2026/07/02) ♡
- Psychosocial Care Utilization Among Patients With Duchenne Muscular Dystrophy. (2026/07/02) ♡
- Report of the multistakeholder drug development round table meeting of the World Duchenne Organization focusing on challenges for clinical development of therapies. (2026/07/01) ♡
- Laboratory or animal researchiNo research in humans yet. Promising in a test tube or in mice unfortunately means nothing for patients. Identification of myokines associated with the pathological stress response in the mdx mouse model of Duchenne muscular dystrophy. (2026/07/01) ♡
- Early Diagnosis of Duchenne Muscular Dystrophy Requires Newborn Screening for CK, and in the Event of Paresis, Relevant Investigations. (2026/07/01) ♡
- Diaphragm-specific effects of L-citrulline in mdx mice highlight its potential as adjuvant of standard therapy in Duchenne muscular dystrophy. (2026/07/01) ♡
- Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy Added to the Newborn Screening Program. (2026/07/01) ♡
- Calcium handling properties and arrhythmia vulnerability of cardiomyocytes from dystrophin-deficient mdx mice. (2026/07/01) ♡
- Decreasing Microtubule Detyrosination Improves Cardiac Mechanics and Sodium Channel Function in Arrhythmogenic Cardiomyopathy. (2026/07/01) ♡
- Cardiac Safety Outcomes in Delandistrogene Moxeparvovec Clinical Trials for Duchenne Muscular Dystrophy with Up to 5 Years of Follow-up. (2026/07/01) ♡
- Long-term outcomes of home mechanical ventilation in Duchenne Muscular Dystrophy - an observational study. (2026/07/01) ♡
- Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Novel DMD Frameshift Variant (p.Leu2017Profs*5) in Spectrin-Like Repeat 16 Expands the Mutational Spectrum of DMD. (2026/07/01) ♡
- Regenerative Index: a method to assess muscle regeneration in patients with Duchenne muscular dystrophy. (2026/07/01) ♡
- Early-stage study (phase 1 or 2)iEarly research in a small group, primarily aimed at safety and dosage. Whether it actually works still needs to be determined afterward. Human Disposition, Metabolism, and Excretion of Sevasemten (EDG-5506), a Selective Modulator of Fast Myosin in Healthy Volunteers. (2026/07/01) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Duchenne Muscular Dystrophy and Delandistrogene Moxeparvovec Gene Therapy in Children: A Systematic Review and Meta-Analysis. (2026/07/01) ♡
- AI-powered therapeutic aptamer drug discovery: Targeting the CT-domain of CTGF for duchenne muscular dystrophy. (2026/07/01) ♡
- Review articleiA summary of what is known about a topic, written by experts. Not compiled according to fixed search rules, so the selection of studies may be biased. Microprotein, macro-effect: DWORF as a therapeutic strategy in heart failure. (2026/07/01) ♡
- Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. Dystrophin-Deficient Muscular Dystrophy in a Jack Russell Terrier With a Large Deletion in the Canine DMD Gene. (2026/07/01) ♡
- Spontaneous rhabdomyosarcomas in Dmd(mdx) rats. (2026/06/30) ♡
- Meta-analysis of clinical trials assessing the safety of pharmacological treatments for muscular degeneration in Duchenne muscular dystrophy. (2026/06/30) ♡
- Description of individual patientsiThe story of one or a couple of patients. Informative, but you cannot infer from it whether something works in general. A female manifesting carrier of DMD with exon 45 deletion: a case report. (2026/06/30) ♡
- Bilateral perifoveal macular ischemia in non-proliferative Duchenne muscular dystrophy-associated retinopathy: a case report. (2026/06/29) ♡
- Duchenne Muscular Dystrophy Under Three Years of Age. (2026/06/27) ♡
- Leflunomide-inhibited STAT1 activity ameliorates intramuscular M1 macrophage infiltration and promotes muscle regeneration in Duchenne muscular dystrophy. (2026/06/26) ♡
- The Use of the Four Square Step Test and the 10-m Walk/Run Test to Determine Fall Risk in Children With Duchenne Muscular Dystrophy. (2026/06/26) ♡
- Treatment with the Nox1/4 inhibitor Setanaxib ameliorates cardiac function in mouse models of Duchenne muscular dystrophy. (2026/06/26) ♡
- Utrophin requires α-Syntrophin to maintain neuromuscular junction integrity in mdx mice. (2026/06/26) ♡
- Post-marketing safety surveillance and signal characterization of the novel dissociative steroid Vamorolone in Duchenne muscular dystrophy: a comparative disproportionality analysis based on FAERS data. (2026/06/26) ♡
- Can ChatGPT provide reliable guidance to families of children with Duchenne Muscular Dystrophy? A dual perspective of parents and experts. (2026/06/25) ♡
- Sex-dependent responses to moderate/low-intensity swimming and loaded ladder-climbing resistance exercise in mdx mice. (2026/06/24) ♡
- Low-dose MyoAAV 2A-mediated delivery of engineered micro-utrophin achieves pan-muscle tissue distribution with elevated muscle function in Duchenne muscular dystrophy. (2026/06/22) ♡
- Transition from pediatric to adult neurology care in Duchenne muscular dystrophy: a national survey of patient and physician experiences. (2026/06/22) ♡
- Stepwise genetic testing strategy identified pathogenic variants in 10 Chinese Duchenne muscular dystrophy patients. (2026/06/19) ♡
- Targeting muscle fibrosis using non-specific collagenase injections destabilizes the basal lamina and induces matrix remodeling. (2026/06/19) ♡
codex.care does not provide medical advice. Always discuss symptoms, medication, and treatment choices with your own healthcare provider.